Resource Library
Published December 18, 2018
Orphan Drugs in the United States: Exclusivity, Pricing and Treated Populations
Published June 1, 2021
FDA’S Accelerated Approval Pathway: A Rare Disease Perspective
Published March 1, 2015
Huntington’s Disease: Emerging Concepts in Diagnosis and Treatment
Published February 1, 2016
2016 Neurological Rare Disease Special Report
Published March 1, 2017
2017 Neurological Rare Disease Special Report
Published March 1, 2018